U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 15:39:51 GMT 2023
Edited
by admin
on Sat Dec 16 15:39:51 GMT 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name scAAV9.U1a.hSGSH
Part WHOLE
Record UNII
V28L3Q0LVZ
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
REBISUFLIGENE ETISPARVOVEC
INN  
Official Name English
SCAAV9.U1A.HSGSH
Common Name English
DNA (SYNTHETIC ADENO-ASSOCIATED VIRUS 9 VECTOR SCAAV9.U1A.HSGSH HUMAN N-SULFOGLUCOSAMINE SULFOHYDROLASE-SPECIFYING)
Common Name English
ABO-102
Common Name English
rebisufligene etisparvovec [INN]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 433714
Created by admin on Sat Dec 16 15:39:51 GMT 2023 , Edited by admin on Sat Dec 16 15:39:51 GMT 2023
Code System Code Type Description
INN
10697
Created by admin on Sat Dec 16 15:39:51 GMT 2023 , Edited by admin on Sat Dec 16 15:39:51 GMT 2023
PRIMARY
NCI_THESAURUS
C171802
Created by admin on Sat Dec 16 15:39:51 GMT 2023 , Edited by admin on Sat Dec 16 15:39:51 GMT 2023
PRIMARY
CAS
1966978-67-5
Created by admin on Sat Dec 16 15:39:51 GMT 2023 , Edited by admin on Sat Dec 16 15:39:51 GMT 2023
PRIMARY
FDA UNII
V28L3Q0LVZ
Created by admin on Sat Dec 16 15:39:51 GMT 2023 , Edited by admin on Sat Dec 16 15:39:51 GMT 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
GENE_EXPRESSION VECTOR REBISUFLIGENE ETISPARVOVEC DNA INSERT Y3N2FNP4YJ