U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 09:46:25 GMT 2025
Edited
by admin
on Wed Apr 02 09:46:25 GMT 2025
Nucleic Acid Type OLIGONUCLEOTIDE
Sequence Origin HUMAN
Sequence Type COMPLETE
Record UNII
UCH3QQH1C0
Record Status FAILED
Record Version
  • Download
Name Type Language
RGLS4326
Preferred Name English
RGLS-4326
Code English
Classification Tree Code System Code
FDA ORPHAN DRUG 750820
Created by admin on Wed Apr 02 09:46:25 GMT 2025 , Edited by admin on Wed Apr 02 09:46:25 GMT 2025
Code System Code Type Description
FDA UNII
UCH3QQH1C0
Created by admin on Wed Apr 02 09:46:25 GMT 2025 , Edited by admin on Wed Apr 02 09:46:25 GMT 2025
PRIMARY
CAS
2229964-07-0
Created by admin on Wed Apr 02 09:46:25 GMT 2025 , Edited by admin on Wed Apr 02 09:46:25 GMT 2025
PRIMARY
PUBCHEM
154824286
Created by admin on Wed Apr 02 09:46:25 GMT 2025 , Edited by admin on Wed Apr 02 09:46:25 GMT 2025
PRIMARY
Sugar Site Range Site Count
1_1-1_2;1_8-1_9 4 / 9
2'-Fluoro-Ribose 1_4-1_6 3 / 9
2'-O-Methyl-Ribose 1_3;1_7 2 / 9
Linkage Site Range Site Count
Phosporothioate 1_2-1_9 8 / 8
Related Record Type Details
TARGET -> INHIBITOR
SALT/SOLVATE -> PARENT
Related Record Type Details
ACTIVE MOIETY