VILTOLARSEN

U.S. Department of Health & Human Services Divider Arrow

National Institutes of Health Divider Arrow

NCATS

Approval Year

Substance Class	Nucleic Acid Created by `admin` on `Wed Apr 02 00:03:13 GMT 2025` Edited by `admin` on `Wed Apr 02 00:03:13 GMT 2025`
Nucleic Acid Type	OLIGONUCLEOTIDE
Sequence Origin	SYNTHETIC
Sequence Type	COMPLETE
Record UNII	SXA7YP6EKX
Record Status	`Validated (UNII)`
Record Version

Download

Name

Type

Language

VILTOLARSEN

Official Name

English

VILTEPSO

Preferred Name

English

VILTOLARSEN [ORANGE BOOK]

Common Name

English

RNA, (P-DEOXY-P-(DIMETHYLAMINO))(2',3'-DIDEOXY-2',3'-IMINO-2',3'-SECO)(2'A->5')(C-C-M5U-C-C-G-G-M5U-M5U-C-M5U-G-A-A-G-G-M5U-G-M5U-M5U-C)

Common Name

English

Viltolarsen [WHO-DD]

Common Name

English

NCNP-01

Code

English

VILTOLARSEN [JAN]

Common Name

English

viltolarsen [INN]

Common Name

English

NS-065

Code

English

NS-065/NCNP-01

Code

English

VILTOLARSEN [USAN]

Common Name

English

EXON 53 SPECIFIC ANTISENSE MORPHOLINO OLIGONUCLEOTIDE

Common Name

English

ALL-P-AMBO-(2',3'-AZANEDIYL-P,2',3'-TRIDEOXY-P-(DIMETHYLAMINO)-2',3'-SECO)(2'-N->5')(CCTCCGGTTC TGAAGGTGTT C)

Systematic Name

English

Classification Tree Code System Code

FDA ORPHAN DRUG

565616

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

Code System Code Type Description

CAS

2055732-84-6

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

NCI_THESAURUS

C170393

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

WIKIPEDIA

Viltolarsen

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

DRUG BANK

DB15005

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

RXCUI

2389840

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

SMS_ID

100000181739

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

FDA UNII

SXA7YP6EKX

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

INN

10771

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

DAILYMED

SXA7YP6EKX

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

USAN

FG-170

Created by admin on Wed Apr 02 00:03:13 GMT 2025 , Edited by admin on Wed Apr 02 00:03:13 GMT 2025

PRIMARY

Sugar	Site Range	Site Count
morpholino	1_1-1_21	21 / 21

Linkage	Site Range	Site Count
Phosphoryldimethylamine	1_2-1_21	20 / 20

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