U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 15:35:27 UTC 2023
Edited
by admin
on Sat Dec 16 15:35:27 UTC 2023
Nucleic Acid Type OLIGONUCLEOTIDE
Nucleic Acid Subtype ANTI-SENSE
Sequence Origin HUMAN
Sequence Type COMPLETE
Record UNII
SVT2GC4GOI
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Opemalirsen
INN  
Official Name English
opemalirsen [INN]
Common Name English
DNA, d(P-thio)([2′,5′-anhydro-6′-deoxy-4′-C-(hydroxymethyl)-α-L-mannofurano]m5rU-(3′→4′)-[2′,5′-anhydro-6′-deoxy-4′-C-(hydroxymethyl)-α-L-mannofurano]m5rU-(3′→4′)-[2′,5′-anhydro-6′-deoxy-4′-C-(hydroxymethyl)-α-L-man
Common Name English
Code System Code Type Description
CAS
2639853-99-7
Created by admin on Sat Dec 16 15:35:27 UTC 2023 , Edited by admin on Sat Dec 16 15:35:27 UTC 2023
PRIMARY
INN
12631
Created by admin on Sat Dec 16 15:35:27 UTC 2023 , Edited by admin on Sat Dec 16 15:35:27 UTC 2023
PRIMARY
FDA UNII
SVT2GC4GOI
Created by admin on Sat Dec 16 15:35:27 UTC 2023 , Edited by admin on Sat Dec 16 15:35:27 UTC 2023
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_4-1_12 9 / 16
1_1-1_3;1_13-1_15 6 / 16
2'-O-Methoxyethyl ribose 1_16 1 / 16
Linkage Site Range Site Count
Phosporothioate 1_2-1_16 15 / 15
Related Record Type Details
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY