U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 13:50:23 GMT 2025
Edited
by admin
on Wed Apr 02 13:50:23 GMT 2025
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE
Source Materials Parent
Part bone marrow; blood
Fraction Name hematopoietic stem and progenitor cells
Record UNII
SMN5E7TJ9C
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
ETUVETIDIGENE AUTOTEMCEL
INN  
Official Name English
AUTOLOGOUS CD34+ HEMATOPOIETIC STEM AND PROGENITOR CELLS (HSPC), OBTAINED FROM BONE MARROW OR MOBILISED PERIPHERAL BLOOD. THE CELLS ARE TRANSDUCED EX VIVO WITH A SELF-INACTIVATING (SIN), REPLICATION-INCOMPETENT HUMAN IMMUNODEFICIENCY VIRUS 1 (HIV-1) BASE
Preferred Name English
etuvetidigene autotemcel [INN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C184832
Created by admin on Wed Apr 02 13:50:23 GMT 2025 , Edited by admin on Wed Apr 02 13:50:23 GMT 2025
PRIMARY
INN
11283
Created by admin on Wed Apr 02 13:50:23 GMT 2025 , Edited by admin on Wed Apr 02 13:50:23 GMT 2025
PRIMARY
SMS_ID
300000023171
Created by admin on Wed Apr 02 13:50:23 GMT 2025 , Edited by admin on Wed Apr 02 13:50:23 GMT 2025
PRIMARY
FDA UNII
SMN5E7TJ9C
Created by admin on Wed Apr 02 13:50:23 GMT 2025 , Edited by admin on Wed Apr 02 13:50:23 GMT 2025
PRIMARY
Related Record Type Details
TARGET->GENE REPLACEMENT
Related Record Type Details
ACTIVE MOIETY

Agent Modifications

Modification Process Modification Role Modification Type Amount Fragment Name Fragment ID
LENTIVIRAL TRANSFECTION ERETIDIGENE VELENTIVEC LYB908LP8T
Name Property Type Amount Referenced Substance Defining Parameters References
ANTIGEN EXPRESSED BIOLOGICAL
ANTIGEN EXPRESSED BIOLOGICAL
AM9TU3H9K5
Unknown Structure
PROMININ-1
(not present in database)
ANTIGEN EXPRESSED BIOLOGICAL