U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 10:18:08 GMT 2025
Edited
by admin
on Wed Apr 02 10:18:08 GMT 2025
Source Materials Class ORGANISM
Source Materials Type ALLOGENIC HUMAN
Source Materials Parent
Part bone marrow
Fraction Name hematopoietic stem cell, cd34+ stem cells fraction
Record UNII
RZ8DCR7A94
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
AVR-RD-01
Preferred Name English
voxeralgagene autotemcel
INN  
Official Name English
voxeralgagene autotemcel [INN]
Common Name English
VOXERALGAGENE AUTOTEMCEL [USAN]
Common Name English
Autologous CD34+ hematopoietic stem cells (HSCs) transduced ex vivo with a self-inactivating lentiviral vector encoding human alpha-galactosidase A (GLA). Autologous CD34+ hematopoietic stem cells (HSCs) obtained by apheresis, transduced with a non-repli
Common Name English
Code System Code Type Description
USAN
KL-71
Created by admin on Wed Apr 02 10:18:08 GMT 2025 , Edited by admin on Wed Apr 02 10:18:08 GMT 2025
PRIMARY
SMS_ID
300000018727
Created by admin on Wed Apr 02 10:18:08 GMT 2025 , Edited by admin on Wed Apr 02 10:18:08 GMT 2025
PRIMARY
FDA UNII
RZ8DCR7A94
Created by admin on Wed Apr 02 10:18:08 GMT 2025 , Edited by admin on Wed Apr 02 10:18:08 GMT 2025
PRIMARY
NCI_THESAURUS
C188780
Created by admin on Wed Apr 02 10:18:08 GMT 2025 , Edited by admin on Wed Apr 02 10:18:08 GMT 2025
PRIMARY
INN
11441
Created by admin on Wed Apr 02 10:18:08 GMT 2025 , Edited by admin on Wed Apr 02 10:18:08 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY
Name Property Type Amount Referenced Substance Defining Parameters References
ANTIGEN EXPRESSED BIOLOGICAL