Lunsotogene parvec 5' vector

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 17:27:03 GMT 2025` Edited by `admin` on `Wed Apr 02 17:27:03 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	RECOMBINANT VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus a
Infraspecific Type	RECOMBINANT VECTOR
Infraspecific Name	AAV1-ITR/Myo15/5'hOtof/SD/AP/ITR
Part	whole
Record UNII	RVA7BZJ6FH
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

Lunsotogene parvec 5' vector

Common Name

English

Capsomere, recombinant adeno-associated virus 1 viral capsid protein VP1-VP2-VP3 complex (1:1:10), hexacontamer, complex with DNA (recombinant adeno-associated virus vector DB-OTO-5 synthetic gene Myo15 promoter region plus human otoferlin isoform 5 gene

Preferred Name

English

Code System Code Type Description

FDA UNII

RVA7BZJ6FH

Created by admin on Wed Apr 02 17:27:03 GMT 2025 , Edited by admin on Wed Apr 02 17:27:03 GMT 2025

PRIMARY

CAS

2906175-09-3

Created by admin on Wed Apr 02 17:27:03 GMT 2025 , Edited by admin on Wed Apr 02 17:27:03 GMT 2025

PRIMARY

Structural Modifications

Modification Type	Location Site	Location Type	Residue Modified	Extent	Fragment Name	Fragment Approval
INSERTED GENE EXPRESSION VECTOR					Lunsotogene parvec 5' vector transgene insert	GK55MMJ6LS
VIRAL CAPSID					Lunsotogene parvec capsid	5ZU8Y5Q638