U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 10:41:06 GMT 2025
Edited
by admin
on Wed Apr 02 10:41:06 GMT 2025
Source Materials Class ORGANISM
Source Materials Type ALLOGENIC HUMAN
Source Materials State LIVE GENETICALLY MODIFIED
Source Materials Parent
Part whole
Record UNII
Q7V7NYG6GM
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Revakinagene Taroretcel
USAN   INN  
Official Name English
Allogeneic human adult retinal pigment epithelial (RPE) cell line stably transfected with a plasmid encoding human ciliary neurotrophic factor (CNTF). An allogeneic human adult retinal pigment epithelial (RPE) cell line stably transfected with a plasmid
Preferred Name English
NTC-201-6A
Code English
revakinagene taroretcel [INN]
Common Name English
REVAKINAGENE TARORETCEL [USAN]
Common Name English
Code System Code Type Description
SMS_ID
300000013204
Created by admin on Wed Apr 02 10:41:06 GMT 2025 , Edited by admin on Wed Apr 02 10:41:06 GMT 2025
PRIMARY
INN
11375
Created by admin on Wed Apr 02 10:41:06 GMT 2025 , Edited by admin on Wed Apr 02 10:41:06 GMT 2025
PRIMARY
NCI_THESAURUS
C180656
Created by admin on Wed Apr 02 10:41:06 GMT 2025 , Edited by admin on Wed Apr 02 10:41:06 GMT 2025
PRIMARY
USAN
LM-47
Created by admin on Wed Apr 02 10:41:06 GMT 2025 , Edited by admin on Wed Apr 02 10:41:06 GMT 2025
PRIMARY
FDA UNII
Q7V7NYG6GM
Created by admin on Wed Apr 02 10:41:06 GMT 2025 , Edited by admin on Wed Apr 02 10:41:06 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY
cell-based gene therapy (macular telangiectasia type II)

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
PLASMID REVAKINAGENE TARORETCEL PLASMID J3LVA7RZT2