U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 12:26:31 GMT 2025
Edited
by admin
on Wed Apr 02 12:26:31 GMT 2025
Nucleic Acid Type RNAI
Sequence Origin SYNTHETIC
Sequence Type COMPLETE
Record UNII
PX4Q8LA7G6
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
SYL-1001 SODIUM
Preferred Name English
Tivanisiran Sodium
INN   USAN  
Official Name English
RNA, (A-A-G-C-G-C-A-U-C-U-U-C-U-A-C-U-U-C-A), sodium salt, complex with RNA (U-G-A-A-G-U-A-G-A-A-G-A-U-G-C-G-C-U-U) sodium salt (1:18:1:18)
Systematic Name English
Duplex of adenylyl-(3'?5')-adenylyl-(3'?5')-guanylyl-(3'?5')-cytidylyl-(3'?5')-guanylyl-(3'?5')-cytidylyl-(3'?5')-adenylyl-(3'?5')-uridylyl-(3'?5')-cytidylyl-(3'?5')-uridylyl-(3'?5')-uridylyl-(3'?5')-cytidylyl-(3'?5')-uridylyl-(3'?5')-adenylyl-(3'?5')-cy
Systematic Name English
SYL1001 SODIUM
Code English
TIVANISIRAN SODIUM [USAN]
Common Name English
Code System Code Type Description
USAN
LM-122
Created by admin on Wed Apr 02 12:26:31 GMT 2025 , Edited by admin on Wed Apr 02 12:26:31 GMT 2025
PRIMARY
FDA UNII
PX4Q8LA7G6
Created by admin on Wed Apr 02 12:26:31 GMT 2025 , Edited by admin on Wed Apr 02 12:26:31 GMT 2025
PRIMARY
CAS
1848239-71-3
Created by admin on Wed Apr 02 12:26:31 GMT 2025 , Edited by admin on Wed Apr 02 12:26:31 GMT 2025
PRIMARY
NCI_THESAURUS
C203142
Created by admin on Wed Apr 02 12:26:31 GMT 2025 , Edited by admin on Wed Apr 02 12:26:31 GMT 2025
PRIMARY
SMS_ID
300000054725
Created by admin on Wed Apr 02 12:26:31 GMT 2025 , Edited by admin on Wed Apr 02 12:26:31 GMT 2025
PRIMARY
Sugar Site Range Site Count
D-Ribose (RNA) 1_1-1_19;2_1-2_19 38 / 38
Linkage Site Range Site Count
1_2-1_19;2_2-2_19 36 / 36
Related Record Type Details
PARENT -> SALT/SOLVATE