U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 14:34:25 GMT 2025
Edited
by admin
on Wed Apr 02 14:34:25 GMT 2025
Nucleic Acid Type OLIGONUCLEOTIDE
Record UNII
PTC9GTD4E7
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Salanersen
USAN  
Official Name English
RNA, [2?-O-(2-methylamino)-2-oxoethyl](m5C-sp-A-m5C-sp-m5U-m5U-sp-m5U-sp-m5C-sp-A-sp-m5U-sp-A-sp-A-sp-m5U-sp-G-sp-m5C-sp-m5U-sp-G-sp-G-sp-m5C)
Preferred Name English
all-P-ambo-(5'?3')-[2?-O-(2-Methylamino)-2-oxoethyl]-P-thiocytidylyl-(5'?3')-[2?-O-(2-methylamino)-2-oxoethyl]adenylyl-(5'?3')-[2?-O-(2-methylamino)-2-oxoethyl]-P-thio[(5-methyl)cytidylyl)]-(5'?3')-[2?-O-(2-methylamino)-2-oxoethyl]-[(5-methyl)uridylyl-)]
Common Name English
SALANERSEN [USAN]
Common Name English
Code System Code Type Description
FDA UNII
PTC9GTD4E7
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
USAN
LM-200
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
NCI_THESAURUS
C206983
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
CAS
2701584-16-7
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
SMS_ID
300000043679
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
INN
13182
Created by admin on Wed Apr 02 14:34:25 GMT 2025 , Edited by admin on Wed Apr 02 14:34:25 GMT 2025
PRIMARY
Sugar Site Range Site Count
2-(methylamino)acetamide (GeneTools 5'-cap for PMO) 1_1-1_18 18 / 18
Linkage Site Range Site Count
Phosporothioate 1_2;1_4;1_6-1_18 15 / 17
Phosphate 1_3;1_5 2 / 17
Related Record Type Details
SALT/SOLVATE -> PARENT
TARGET->CORRECTOR
Related Record Type Details
ACTIVE MOIETY