Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 10:00:38 GMT 2025
by
admin
on
Wed Apr 02 10:00:38 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE SELF-COMPLEMENTARY NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus a |
| Author | NONE |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | scAAVrh74.MHCK7.hSGCB |
| Part | whole |
| Record UNII |
NM4FH5S2OW
|
| Record Status |
Validated (UNII)
|
| Record Version |
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-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Official Name | English | ||
|
Preferred Name | English | ||
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Common Name | English | ||
|
Common Name | English | ||
|
Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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2365142-14-7
Created by
admin on Wed Apr 02 10:00:38 GMT 2025 , Edited by admin on Wed Apr 02 10:00:38 GMT 2025
|
PRIMARY | |||
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C188604
Created by
admin on Wed Apr 02 10:00:38 GMT 2025 , Edited by admin on Wed Apr 02 10:00:38 GMT 2025
|
PRIMARY | |||
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300000015960
Created by
admin on Wed Apr 02 10:00:38 GMT 2025 , Edited by admin on Wed Apr 02 10:00:38 GMT 2025
|
PRIMARY | |||
|
11619
Created by
admin on Wed Apr 02 10:00:38 GMT 2025 , Edited by admin on Wed Apr 02 10:00:38 GMT 2025
|
PRIMARY | |||
|
NM4FH5S2OW
Created by
admin on Wed Apr 02 10:00:38 GMT 2025 , Edited by admin on Wed Apr 02 10:00:38 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
EXPRESSED PROTEIN->VECTOR |
|
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
LGMD2E patients
|
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| TRANSGENE | UNSPECIFIED SUBSTANCE |
2883a2b5
(not in database)
|