U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 15:10:02 GMT 2023
Edited
by admin
on Sat Dec 16 15:10:02 GMT 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name Recombinant adeno-associated viral vector containing a codon-optimised human coagulation factor IX cDNA
Part WHOLE
Record UNII
L7D6JMC51Y
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
LANACOGENE VOSIPARVOVEC
INN  
Official Name English
lanacogene vosiparvovec [INN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C175806
Created by admin on Sat Dec 16 15:10:02 GMT 2023 , Edited by admin on Sat Dec 16 15:10:02 GMT 2023
PRIMARY
CAS
1939139-26-0
Created by admin on Sat Dec 16 15:10:02 GMT 2023 , Edited by admin on Sat Dec 16 15:10:02 GMT 2023
PRIMARY
INN
10688
Created by admin on Sat Dec 16 15:10:02 GMT 2023 , Edited by admin on Sat Dec 16 15:10:02 GMT 2023
PRIMARY
FDA UNII
L7D6JMC51Y
Created by admin on Sat Dec 16 15:10:02 GMT 2023 , Edited by admin on Sat Dec 16 15:10:02 GMT 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
VECTOR EXPRESSED PROTEIN COAGULATION FACTOR IX HUMAN 6U90Y1795T
GENE_EXPRESSION VECTOR LANACOGENE VOSIPARVOVEC TRANSGENE INSERT G94MQE3S0E