U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 04:25:15 GMT 2025
Edited
by admin
on Wed Apr 02 04:25:15 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name Recombinant adeno-associated viral vector containing a codon-optimised human coagulation factor IX cDNA
Part whole
Record UNII
L7D6JMC51Y
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
LANACOGENE VOSIPARVOVEC
INN  
Official Name English
lanacogene vosiparvovec [INN]
Preferred Name English
Code System Code Type Description
NCI_THESAURUS
C175806
Created by admin on Wed Apr 02 04:25:15 GMT 2025 , Edited by admin on Wed Apr 02 04:25:15 GMT 2025
PRIMARY
SMS_ID
300000011776
Created by admin on Wed Apr 02 04:25:15 GMT 2025 , Edited by admin on Wed Apr 02 04:25:15 GMT 2025
PRIMARY
CAS
1939139-26-0
Created by admin on Wed Apr 02 04:25:15 GMT 2025 , Edited by admin on Wed Apr 02 04:25:15 GMT 2025
PRIMARY
INN
10688
Created by admin on Wed Apr 02 04:25:15 GMT 2025 , Edited by admin on Wed Apr 02 04:25:15 GMT 2025
PRIMARY
FDA UNII
L7D6JMC51Y
Created by admin on Wed Apr 02 04:25:15 GMT 2025 , Edited by admin on Wed Apr 02 04:25:15 GMT 2025
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
GENE_EXPRESSION VECTOR LANACOGENE VOSIPARVOVEC TRANSGENE INSERT G94MQE3S0E