U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 15:35:21 UTC 2023
Edited
by admin
on Sat Dec 16 15:35:21 UTC 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependovirus
Organism Species adeno-associated virus
Author NONE
Infraspecific Type SUBSTRAIN
Infraspecific Name AAV2/5-RPE65P/OPTIRPE65
Part WHOLE
Record UNII
KVF2UY1OR4
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
CEVARETIGENE RITOPARVOVEC
USAN   INN  
Official Name English
cevaretigene ritoparvovec [INN]
Common Name English
AAV2/5-OPTIRPE65
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS 5 VECTOR AAV2/5-OPTIRPE65 HUMAN ALL-TRANS-RETINYL ESTER ISOMEROHYDROLASE CODON-OPTIMIZED GENE RPE65 PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS)
Common Name English
A001
Code English
AAV2/5-RPE65P/OPTIRPE65
Common Name English
CEVARETIGENE RITOPARVOVEC [USAN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C175755
Created by admin on Sat Dec 16 15:35:21 UTC 2023 , Edited by admin on Sat Dec 16 15:35:21 UTC 2023
PRIMARY
FDA UNII
KVF2UY1OR4
Created by admin on Sat Dec 16 15:35:21 UTC 2023 , Edited by admin on Sat Dec 16 15:35:21 UTC 2023
PRIMARY
INN
11368
Created by admin on Sat Dec 16 15:35:21 UTC 2023 , Edited by admin on Sat Dec 16 15:35:21 UTC 2023
PRIMARY
CAS
2247971-00-0
Created by admin on Sat Dec 16 15:35:21 UTC 2023 , Edited by admin on Sat Dec 16 15:35:21 UTC 2023
PRIMARY
USAN
GH-111
Created by admin on Sat Dec 16 15:35:21 UTC 2023 , Edited by admin on Sat Dec 16 15:35:21 UTC 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR