Clemidsogene Lanparvovec

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 07:50:18 GMT 2025` Edited by `admin` on `Wed Apr 02 07:50:18 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus a
Infraspecific Type	RECOMBINANT VECTOR
Infraspecific Name	AAV9.CB7.HIDS
Part	whole
Record UNII	K5LW2WBP48
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

Clemidsogene Lanparvovec

Official Name

English

RGX-121

Preferred Name

English

Recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding human iduronate 2-sulfatase (IDS, ?-L-iduronate sulfate sulfatase) under control of a human cytomegalovirus (CMV) immediate-early enhancer/chicken ?-actin (CBA) promot

Common Name

English

CLEMIDSOGENE LANPARVOVEC [USAN]

Common Name

English

clemidsogene lanparvovec [INN]

Common Name

English

DNA (recombinant replication-defective adeno-associated virus 9 vector RGX-121 cytomegalovirus immediate-early promoter-enhancer plus chicken ?-actin promoter plus chicken ?-actin intron plus human iduronate-2-sulfatase gene plus rabbit ?-globin polyaden

Common Name

English

Code System Code Type Description

SMS_ID

300000001341