U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 13:39:14 GMT 2023
Edited
by admin
on Sat Dec 16 13:39:14 GMT 2023
Nucleic Acid Type OLIGONUCLEOTIDE
Nucleic Acid Subtype
Record UNII
JAC5IJI520
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
BALIFORSEN SODIUM
Common Name English
IONIS-598769
Code English
Code System Code Type Description
FDA UNII
JAC5IJI520
Created by admin on Sat Dec 16 13:39:14 GMT 2023 , Edited by admin on Sat Dec 16 13:39:14 GMT 2023
PRIMARY
PUBCHEM
121488174
Created by admin on Sat Dec 16 13:39:14 GMT 2023 , Edited by admin on Sat Dec 16 13:39:14 GMT 2023
PRIMARY
CAS
1687746-79-7
Created by admin on Sat Dec 16 13:39:14 GMT 2023 , Edited by admin on Sat Dec 16 13:39:14 GMT 2023
PRIMARY
Sugar Site Range Site Count
2'-O-Methoxyethyl ribose 1_1-1_2;1_15-1_16 4 / 16
Deoxyribose (DNA) 1_5-1_12 8 / 16
1_3-1_4;1_13-1_14 4 / 16
Linkage Site Range Site Count
Sodium Phosporothioate 1_2-1_16 15 / 15
Related Record Type Details
PARENT -> SALT/SOLVATE
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
NUCLEOSIDE_SUBSTITUTION [1_2] [1_15] SITE_SPECIFIC 2'-O-(2-METHOXYETHYL)-5-METHYLCYTIDINE AOQ54IZZ6J
NUCLEOSIDE_SUBSTITUTION [1_3] [1_4] [1_11] [1_12] SITE_SPECIFIC 2'-O,4'-C-((1S)-ETHANE-1,1-DIYL).BETA.-D-RIBOSE 5-METHYL CYTIDINE 7XRE49320R
NUCLEOSIDE_SUBSTITUTION [1_1] 5'-TERMINUS 2'-O-(2-METHOXYETHYL)-5-METHYLURIDINE 9Q36I4D9VB