U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 01:50:37 GMT 2025
Edited
by admin
on Wed Apr 02 01:50:37 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependovirus
Organism Species adeno-associated virus
Author NONE
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name AAV2/5-HRKP.RPGR
Part whole
Record UNII
IIO8Q82SD1
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
AAV-RPGR
Preferred Name English
BOTARETIGENE SPAROPARVOVEC
USAN  
Official Name English
Botaretigene sparoparvovec [WHO-DD]
Common Name English
DNA (RECOMBINANT PSEUDOTYPED ADENO-ASSOCIATED VIRUS 5 VECTOR AAV-RPGR HUMAN RHODOPSIN KINASE PROMOTER FRAGMENT-REGULATED HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR RPGR-ORF15 ISOFORM GENE VARIANT PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FL
Common Name English
BOTARETIGENE SPAROPARVOVEC [USAN]
Common Name English
botaretigene sparoparvovec [INN]
Common Name English
Code System Code Type Description
INN
12076
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
USAN
JK-78
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
CAS
2417551-39-2
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
NCI_THESAURUS
C188587
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
SMS_ID
100000183208
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
FDA UNII
IIO8Q82SD1
Created by admin on Wed Apr 02 01:50:37 GMT 2025 , Edited by admin on Wed Apr 02 01:50:37 GMT 2025
PRIMARY
Related Record Type Details
ACTIVE MOIETY