FORDADISTROGENE MOVAPARVOVEC

Investigational

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 06:46:26 GMT 2025` Edited by `admin` on `Wed Apr 02 06:46:26 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	VIRUS
Source Materials State	LIVE GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus a
Infraspecific Type	SUBSTRAIN
Infraspecific Name	AAV2(ITR)AAV9.HCK.OPTI-DYS.DELTA.3978
Part	whole
Record UNII	H4T32JIH01
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

FORDADISTROGENE MOVAPARVOVEC

Official Name

English

PF-06939926

Preferred Name

English

PF-06939926 IS A RECOMBINANT AAV VECTOR CONTAINING THE AAV SEROTYPE 9 (AAV9) CAPSID PACKAGING A MINIATURIZED CODON-OPTIMIZED VERSION OF THE DMD GENE(CALLED OPTI-DYS.DELTA.3978) WHICH ENCODES THE DOMAINS MINIMALLY REQUIRED FOR FUNCTIONALITY OF THE DYSTROP

Common Name

English

FORDADISTROGENE MOVAPARVOVEC [USAN]

Common Name

English

fordadistrogene movaparvovec [INN]

Common Name

English

DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS 9 VECTOR PF-06939926 HUMAN MUSCLE-SPECIFIC ENHANCER/PROMOTER PLUS HUMAN MINI-DYSTROPHIN GENE PLUS ADENO-ASSOCIATED VIRUS 9 INVERTED TERMINAL REPEAT FLANKS)

Common Name

English

AAV9.HCK.OPTI-DYS.DELTA.3978

Common Name

English

Fordadistrogene movaparvovec [WHO-DD]

Common Name

English

Code System Code Type Description

FDA UNII

H4T32JIH01