U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 15:45:38 UTC 2023
Edited
by admin
on Sat Dec 16 15:45:38 UTC 2023
Source Materials Class ORGANISM
Source Materials Type VIRUS
Source Materials State LIVE GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name AAV2(ITR)AAV9.HCK.OPTI-DYS.DELTA.3978
Part WHOLE
Record UNII
H4T32JIH01
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
FORDADISTROGENE MOVAPARVOVEC
USAN   INN  
Official Name English
PF-06939926 IS A RECOMBINANT AAV VECTOR CONTAINING THE AAV SEROTYPE 9 (AAV9) CAPSID PACKAGING A MINIATURIZED CODON-OPTIMIZED VERSION OF THE DMD GENE(CALLED OPTI-DYS.DELTA.3978) WHICH ENCODES THE DOMAINS MINIMALLY REQUIRED FOR FUNCTIONALITY OF THE DYSTROP
Common Name English
FORDADISTROGENE MOVAPARVOVEC [USAN]
Common Name English
fordadistrogene movaparvovec [INN]
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS 9 VECTOR PF-06939926 HUMAN MUSCLE-SPECIFIC ENHANCER/PROMOTER PLUS HUMAN MINI-DYSTROPHIN GENE PLUS ADENO-ASSOCIATED VIRUS 9 INVERTED TERMINAL REPEAT FLANKS)
Common Name English
AAV9.HCK.OPTI-DYS.DELTA.3978
Common Name English
Fordadistrogene movaparvovec [WHO-DD]
Common Name English
PF-06939926
Code English
Code System Code Type Description
FDA UNII
H4T32JIH01
Created by admin on Sat Dec 16 15:45:38 UTC 2023 , Edited by admin on Sat Dec 16 15:45:38 UTC 2023
PRIMARY
NCI_THESAURUS
C175785
Created by admin on Sat Dec 16 15:45:38 UTC 2023 , Edited by admin on Sat Dec 16 15:45:38 UTC 2023
PRIMARY
USAN
GH-67
Created by admin on Sat Dec 16 15:45:38 UTC 2023 , Edited by admin on Sat Dec 16 15:45:38 UTC 2023
PRIMARY
INN
11362
Created by admin on Sat Dec 16 15:45:38 UTC 2023 , Edited by admin on Sat Dec 16 15:45:38 UTC 2023
PRIMARY
CAS
2248111-37-5
Created by admin on Sat Dec 16 15:45:38 UTC 2023 , Edited by admin on Sat Dec 16 15:45:38 UTC 2023
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
GENE_EXPRESSION VECTOR FORDADISTROGENE MOVAPARVOVEC TRANSGENE INSERT G33XRK212Z