Lunsotogene parvec 5' vector transgene insert

Approval Year

Substance Class	Nucleic Acid Created by `admin` on `Wed Apr 02 17:02:37 GMT 2025` Edited by `admin` on `Wed Apr 02 17:02:37 GMT 2025`
Nucleic Acid Type	VECTOR
Sequence Origin	VIRAL, HUMAN
Sequence Type	COMPLETE
Record UNII	GK55MMJ6LS
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

Lunsotogene parvec 5' vector transgene insert

Common Name

English

DB-OTO-5 transgene insert transgene insert

Preferred Name

English

Recombinant adeno-associated virus vector DB-OTO-5 transgene insert including synthetic gene Myo15 promoter region plus human otoferlin isoform 5 gene 5?-fragment plus synthetic splice donor site plus recombinant alkaline phosphatase gene fragment plus a

Common Name

English

Code System Code Type Description

FDA UNII

GK55MMJ6LS

Created by admin on Wed Apr 02 17:02:37 GMT 2025 , Edited by admin on Wed Apr 02 17:02:37 GMT 2025

PRIMARY

CAS

2905329-49-7

Created by admin on Wed Apr 02 17:02:37 GMT 2025 , Edited by admin on Wed Apr 02 17:02:37 GMT 2025

PRIMARY

Sugar	Site Range	Site Count
Deoxyribose (DNA)	1_1-1_4246	4246 / 4246

Linkage	Site Range	Site Count
Phosphate	1_2-1_4246	4245 / 4245

Name	Property Type	Amount	Referenced Substance	Defining	Parameters	References
5' hOtof (v5)	NUCLEIC ACID FEATURE

3'-ITR	NUCLEIC ACID FEATURE

AP	NUCLEIC ACID FEATURE

SD	NUCLEIC ACID FEATURE

Myo15	NUCLEIC ACID FEATURE

5'-ITR	NUCLEIC ACID FEATURE