U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 17:51:24 GMT 2025
Edited
by admin
on Wed Apr 02 17:51:24 GMT 2025
Nucleic Acid Type VECTOR
Sequence Type COMPLETE
Record UNII
G74YZ2T2M7
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Pivodisgene parvec transgene insert
Common Name English
RGX-202 transgene insert (recombinant replication-defective adeno-associated virus 8 vector RGX-202 synthetic promoter Spc5-12 plus human codon-optimized microdystrophin variant ABD1-H1-R1-R2-R3-H3-R24-H4-CR-CT194 plus synthetic polyadenylation signal pl
Preferred Name English
Code System Code Type Description
FDA UNII
G74YZ2T2M7
Created by admin on Wed Apr 02 17:51:24 GMT 2025 , Edited by admin on Wed Apr 02 17:51:24 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4734 4734 / 4734
Linkage Site Range Site Count
Phosphate 1_2-1_4734 4733 / 4733
Name Property Type Amount Referenced Substance Defining Parameters References
3'-ITR NUCLEIC ACID FEATURE
TRANSGENE NUCLEIC ACID FEATURE
PROMPTER NUCLEIC ACID FEATURE
5'-ITR NUCLEIC ACID FEATURE