U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 19:10:03 GMT 2023
Edited
by admin
on Sat Dec 16 19:10:03 GMT 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Organism Family Parvoviridae
Organism Genus Dependovirus
Organism Species adeno-associated virus
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name gcSCD-AAV6 vector with Sequence homologous to the human HBB gene
Part whole
Record UNII
G2X9QZG8TU
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
NULABEGLOGENE AUTOGEDTEMCEL AAV6 VECTOR
Common Name English
NULABEGLOGENE AUTOGEDTEMCEL AAV6 VECTOR WITH SEQUENCE HOMOLOGOUS TO THE HUMAN HBB GENE
Common Name English
Code System Code Type Description
FDA UNII
G2X9QZG8TU
Created by admin on Sat Dec 16 19:10:03 GMT 2023 , Edited by admin on Sat Dec 16 19:10:03 GMT 2023
PRIMARY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR NULABEGLOGENE AUTOGEDTEMCEL TRANSGENE INSERT KND6MY3R59