U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 10:53:30 GMT 2025
Edited
by admin
on Wed Apr 02 10:53:30 GMT 2025
Nucleic Acid Type OLIGONUCLEOTIDE
Sequence Origin SYNTHETIC
Sequence Type COMPLETE
Record UNII
F77TA4U3SP
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
RUGONERSEN
USAN   INN  
Official Name English
RO-7248824-000
Preferred Name English
all-P-ambo-5-methyl-2'-O,4'-C-methylene-P-thiouridylyl-(3'?5')- 5-methyl-2'-O,4'-C-methylene-P-thiouridylyl-(3'?5')-2'-O,4'-C-methylene-P-thioadenylyl-(3'?5')-2'-deoxy-P-thiocytidylyl- (3'?5')-2'-O,4'-C-methylene-P-thioadenylyl-(3'?5')-2'-deoxy-P-thiocyt
Common Name English
Rugonersen [WHO-DD]
Common Name English
RUGONERSEN [USAN]
Common Name English
RO7248824-000
Code English
rugonersen [INN]
Common Name English
RTR33090 FREE ACID
Code English
RTR-33090 FREE ACID
Code English
DNA, d(P-thio)((2'-O,4'-C-methylene)m5rU-(2'-O,4'-C-methylene)m5rU-(2'-O,4'-C-methylene)rA-C-(2'-O,4'-C-methylene)rA-C-T-T-A-A-T-T-A-T-A-C-T-(2'-O,4'-C-methylene)m5rU-(2'-O,4'-C-methylene)m5rC-(2'-O,4'-C-methylene)m5rC)
Common Name English
all-P-ambo-5-methyl-2'-O,4'-C-methylene-P-thiouridylyl-(3'?5')- 5-methyl-2'-O,4'- C-methylene-P-thiouridylyl-(3'?5')-2'-O,4'-C-methylene-P-thioadenylyl-(3'?5')-2'- deoxy-P-thiocytidylyl- (3'?5')-2'-O,4'-C-methylene-P-thioadenylyl-(3'?5')-2'- deoxy-P-thio
Common Name English
Code System Code Type Description
FDA UNII
F77TA4U3SP
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
CAS
2591587-57-2
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
INN
11779
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
NCI_THESAURUS
C184816
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
SMS_ID
300000013243
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
USAN
KL-63
Created by admin on Wed Apr 02 10:53:30 GMT 2025 , Edited by admin on Wed Apr 02 10:53:30 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_4;1_6-1_17 13 / 20
1_1-1_3;1_5;1_18-1_20 7 / 20
Linkage Site Range Site Count
Phosporothioate 1_2-1_20 19 / 19
Related Record Type Details
SALT/SOLVATE -> PARENT
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
NUCLEOSIDE BASE SUBSTITUTION [1_1] [1_2] SITE_SPECIFIC THYMINE QR26YLT7LT
NUCLEOSIDE BASE SUBSTITUTION [1_19] [1_20] SITE_SPECIFIC 5-METHYLCYTOSINE 6R795CQT4H