U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 17:55:55 GMT 2023
Edited
by admin
on Sat Dec 16 17:55:55 GMT 2023
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name scAAV .rh74.tMCK.hSGCA
Part WHOLE
Record UNII
F31AI96DHK
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
PATIDISTROGENE BEXOPARVOVEC
INN   USAN  
Official Name English
RECOMBINANT SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS AAVRH74 VECTOR SRP-9004 TMCK PROMOTER PLUS HUMAN .ALPHA.-SARCOGLYCAN-SPECIFYING
Common Name English
SRP-9004
Code English
patidistrogene bexoparvovec [INN]
Common Name English
PATIDISTROGENE BEXOPARVOVEC [USAN]
Common Name English
Code System Code Type Description
CAS
2376210-48-7
Created by admin on Sat Dec 16 17:55:55 GMT 2023 , Edited by admin on Sat Dec 16 17:55:55 GMT 2023
PRIMARY
INN
11593
Created by admin on Sat Dec 16 17:55:55 GMT 2023 , Edited by admin on Sat Dec 16 17:55:55 GMT 2023
PRIMARY
FDA UNII
F31AI96DHK
Created by admin on Sat Dec 16 17:55:55 GMT 2023 , Edited by admin on Sat Dec 16 17:55:55 GMT 2023
PRIMARY
NCI_THESAURUS
C184857
Created by admin on Sat Dec 16 17:55:55 GMT 2023 , Edited by admin on Sat Dec 16 17:55:55 GMT 2023
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY
for alpha-sarcoglycan deficiency

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
TRANSGENE UNSPECIFIED SUBSTANCE
820ad9c2
(not in database)