Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 11:56:29 GMT 2025
by
admin
on
Wed Apr 02 11:56:29 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | AUTOLOGOUS HUMAN |
| Source Materials State | LIVE GENETICALLY MODIFIED |
| Source Materials Parent | |
| Part | bone marrow |
| Fraction Name | hematopoietic stem and progenitor cells |
| Record UNII |
EPP8G99QG4
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Preferred Name | English | ||
|
Official Name | English | ||
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Common Name | English | ||
|
Common Name | English | ||
|
Common Name | English | ||
|
Code | English | ||
|
Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
EPP8G99QG4
Created by
admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
|
PRIMARY | |||
|
11282
Created by
admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
|
PRIMARY | |||
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JK-136
Created by
admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
|
PRIMARY | |||
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C180638
Created by
admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
|
PRIMARY | |||
|
300000000100
Created by
admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
TARGET->ENZYME REPLACEMENT |
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| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
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Agent Modifications
| Modification Process | Modification Role | Modification Type | Amount | Fragment Name | Fragment ID |
|---|---|---|---|---|---|
| CULTURE | CD34+ ENRICHMENT | BIOLOGICAL | UNSPECIFIED SUBSTANCE | 9cd8c8f9 | |
| LENTIVIRAL TRANSFECTION | TRANSFECTION | BIOLOGICAL | UNSPECIFIED SUBSTANCE | f1852827 |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| GENE_EXPRESSION VECTOR | ATIDARSAGENE AUTOTEMCEL PROVIRUS SEQUENCE | KZU38SJ6BG | ||||
| VECTOR EXPRESSED PROTEIN | ATIDARSAGENE AUTOTEMCEL HUMAN ARYLSULFATASE A PREPROTEIN | VG44W4V6XH | ||||
| VECTOR EXPRESSED PROTEIN | ARYLSULFATASE A | EJS32ZO2L4 |
| Name | Property Type | Amount | Referenced Substance | Defining | Parameters | References |
|---|---|---|---|---|---|---|
| ANTIGEN EXPRESSED | BIOLOGICAL |
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| ANTIGEN EXPRESSED | BIOLOGICAL |
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| ANTIGEN NOT EXPRESSED | BIOLOGICAL |
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| ANTIGEN EXPRESSED | BIOLOGICAL |
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AM9TU3H9K5
PROMININ-1
(not present in database)
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| ANTIGEN NOT EXPRESSED | BIOLOGICAL |
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| ANTIGEN NOT EXPRESSED | BIOLOGICAL |
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| ANTIGEN EXPRESSED | BIOLOGICAL |
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| ANTIGEN NOT EXPRESSED | BIOLOGICAL |
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| ANTIGEN EXPRESSED | BIOLOGICAL |
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