Approval Year
Substance Class |
Nucleic Acid
Created
by
admin
on
Edited
Sat Dec 16 17:19:46 GMT 2023
by
admin
on
Sat Dec 16 17:19:46 GMT 2023
|
Nucleic Acid Type | MRNA |
Nucleic Acid Subtype | ANTI-SENSE |
Sequence Origin | SYNTHETIC |
Sequence Type | COMPLETE |
Record UNII |
AXQ9493NT2
|
Record Status |
Validated (UNII)
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Record Version |
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-
Download
Name | Type | Language | ||
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Official Name | English | ||
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Code | English | ||
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Common Name | English | ||
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Common Name | English | ||
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Common Name | English |
Code System | Code | Type | Description | ||
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11915
Created by
admin on Sat Dec 16 17:19:46 GMT 2023 , Edited by admin on Sat Dec 16 17:19:46 GMT 2023
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PRIMARY | |||
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HI-42
Created by
admin on Sat Dec 16 17:19:46 GMT 2023 , Edited by admin on Sat Dec 16 17:19:46 GMT 2023
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PRIMARY | |||
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AXQ9493NT2
Created by
admin on Sat Dec 16 17:19:46 GMT 2023 , Edited by admin on Sat Dec 16 17:19:46 GMT 2023
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PRIMARY | |||
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2305355-56-8
Created by
admin on Sat Dec 16 17:19:46 GMT 2023 , Edited by admin on Sat Dec 16 17:19:46 GMT 2023
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PRIMARY | |||
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C186394
Created by
admin on Sat Dec 16 17:19:46 GMT 2023 , Edited by admin on Sat Dec 16 17:19:46 GMT 2023
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PRIMARY |
Sugar | Site Range | Site Count |
---|---|---|
Deoxyribose (DNA) | 1_7-1_16 | 10 / 20 |
2'-O-Methoxyethyl ribose | 1_1-1_6;1_17-1_20 | 10 / 20 |
Linkage | Site Range | Site Count |
---|---|---|
Phosphate | 1_3-1_7;1_18 | 6 / 19 |
Phosporothioate | 1_2;1_8-1_17;1_19-1_20 | 13 / 19 |
Related Record | Type | Details | ||
---|---|---|---|---|
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SALT/SOLVATE -> PARENT |
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EXPRESSED PROTEIN->VECTOR |
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Related Record | Type | Details | ||
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ACTIVE MOIETY |
For the treatment of Alexander disease (AxD)
|
Structural Modifications
Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
---|---|---|---|---|---|---|
NUCLEOSIDE BASE SUBSTITUTION | [1_4] [1_6] | SITE_SPECIFIC | THYMINE | QR26YLT7LT | ||
NUCLEOSIDE BASE SUBSTITUTION | [1_1] [1_9] [1_10] [1_12] [1_15] [1_20] | SITE_SPECIFIC | 5-METHYLCYTOSINE | 6R795CQT4H |