ZILDISTROGENE VAROPARVOVEC

U.S. Department of Health & Human Services Divider Arrow

National Institutes of Health Divider Arrow

NCATS

Investigational

Investigational

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 00:45:02 GMT 2025` Edited by `admin` on `Wed Apr 02 00:45:02 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependovirus
Organism Species	adeno-associated virus
Infraspecific Type	SUBSTRAIN
Infraspecific Name	RAAV REP2-CAP9-CK8-H-.MU.D5
Part	whole
Record UNII	ASM9NQ89TK
Record Status	`Validated (UNII)`
Record Version

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Name

Type

Language

A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/9 (RAAV REP2-CAP9) VECTOR, ENCODING HUMAN MICRODYSTROPHIN 5 (H-.MU.D5) UNDER CONTROL OF CK8 MUSCLE CREATINE KINASE PROMOTER AND ENHANCER ELEMENTS

Preferred Name

English

ZILDISTROGENE VAROPARVOVEC

Official Name

English

zildistrogene varoparvovec [INN]

Common Name

English

Code System Code Type Description

CAS

2220231-04-7

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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NCI_THESAURUS

C171806

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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CLINICAL_TRIALS.GOV

NCT03368742

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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FDA UNII

ASM9NQ89TK

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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SMS_ID

100000183644

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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INN

11088

Created by admin on Wed Apr 02 00:45:02 GMT 2025 , Edited by admin on Wed Apr 02 00:45:02 GMT 2025

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Related Record Type Details


					ASM9NQ89TK

ZILDISTROGENE VAROPARVOVEC

ACTIVE MOIETY

Amount:

Agent Modifications

Modification Process	Modification Role	Modification Type	Amount	Fragment Name	Fragment ID
INACTIVATION		CHEMICAL

Structural Modifications

Modification Type	Location Site	Location Type	Residue Modified	Extent	Fragment Name	Fragment Approval
INSERTED GENE EXPRESSION VECTOR					ZILDISTROGENE VAROPARVOVEC RAAV9-CK8-H-MU D5 CONSTRUCT	7MZW6BJA64