NULABEGLOGENE AUTOGEDTEMCEL SINGLE GUIDE RNA SEQUENCE TARGETING THE FIRST EXON OF THE HUMAN .BETA.-GLOBIN (HBB) GENE

Substance Class	Nucleic Acid Created by `admin` on `Wed Apr 02 10:18:06 GMT 2025` Edited by `admin` on `Wed Apr 02 10:18:06 GMT 2025`
Nucleic Acid Type	CRISPR GUIDE SEQUENCE
Sequence Type	COMPLETE
Record UNII	AAC95PP873
Record Status	`Validated (UNII)`
Record Version

Name

Type

Language

Preferred Name

English

Code System Code Type Description

FDA UNII

AAC95PP873

Created by admin on Wed Apr 02 10:18:06 GMT 2025 , Edited by admin on Wed Apr 02 10:18:06 GMT 2025

PRIMARY

Sugar	Site Range	Site Count
D-Ribose (RNA)	1_1-1_20	20 / 20

Linkage	Site Range	Site Count
Phosphate	1_2-1_20	19 / 19