U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 18:09:20 GMT 2023
Edited
by admin
on Sat Dec 16 18:09:20 GMT 2023
Nucleic Acid Type CRISPR GUIDE SEQUENCE
Nucleic Acid Subtype
Sequence Type COMPLETE
Record UNII
AAC95PP873
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
NULABEGLOGENE AUTOGEDTEMCEL SINGLE GUIDE RNA SEQUENCE TARGETING THE FIRST EXON OF THE HUMAN .BETA.-GLOBIN (HBB) GENE
Common Name English
Code System Code Type Description
FDA UNII
AAC95PP873
Created by admin on Sat Dec 16 18:09:20 GMT 2023 , Edited by admin on Sat Dec 16 18:09:20 GMT 2023
PRIMARY
Sugar Site Range Site Count
D-Ribose (RNA) 1_1-1_20 20 / 20
Linkage Site Range Site Count
Phosphate 1_2-1_20 19 / 19