U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 20:09:10 GMT 2025
Edited
by admin
on Wed Apr 02 20:09:10 GMT 2025
Nucleic Acid Type VECTOR
Sequence Origin VIRAL, HUMAN
Sequence Type COMPLETE
Record UNII
99FXQ4ZT3J
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Lonimecgene renparvovec trangene insert
Preferred Name English
Code System Code Type Description
FDA UNII
99FXQ4ZT3J
Created by admin on Wed Apr 02 20:09:10 GMT 2025 , Edited by admin on Wed Apr 02 20:09:10 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_3214 3214 / 3214
Linkage Site Range Site Count
Phosphate 1_2-1_3214 3213 / 3213
Name Property Type Amount Referenced Substance Defining Parameters References
wtITR NUCLEIC ACID FEATURE
mMEP426 Promoter NUCLEIC ACID FEATURE
miRARE NUCLEIC ACID FEATURE
miniMeCP2 (antisense) NUCLEIC ACID FEATURE
Portion of RDH1pA with 3 miRNA targets NUCLEIC ACID FEATURE
wtITR (antisense) NUCLEIC ACID FEATURE
miniMeCP2 (antisense) NUCLEIC ACID FEATURE
mutITR NUCLEIC ACID FEATURE
Distal pA fragment with miR-124 target NUCLEIC ACID FEATURE
Pichinde VirusmiRARE (antisense) NUCLEIC ACID FEATURE
Portion of RDH1pA with 3 miRNA targets (antisense) NUCLEIC ACID FEATURE
miniMeCP2 NUCLEIC ACID FEATURE