Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 05:14:19 GMT 2025
by
admin
on
Wed Apr 02 05:14:19 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependovirus |
| Organism Species | adeno-associated virus |
| Author | NONE |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | rAAV8-TBG-hUGT1A1 |
| Part | whole |
| Record UNII |
8WI5RJ8D9V
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Preferred Name | English | ||
|
Official Name | English | ||
|
Code | English | ||
|
Common Name | English | ||
|
Code | English | ||
|
Code | English | ||
|
Systematic Name | English | ||
|
Common Name | English |
| Classification Tree | Code System | Code | ||
|---|---|---|---|---|
|
EU-Orphan Drug |
EU/3/16/1772
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
300000005907
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY | |||
|
10921
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY | |||
|
2092457-20-8
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY | |||
|
EF-156
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY | |||
|
8WI5RJ8D9V
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY | |||
|
C171805
Created by
admin on Wed Apr 02 05:14:19 GMT 2025 , Edited by admin on Wed Apr 02 05:14:19 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
VECTOR->EXPRESSED PROTEIN |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| VECTOR EXPRESSED PROTEIN | URIDINE DIPHOSPHATE GLUCURONOSYLTRANSFERASE 1A1 | 0RFO7VC96N | ||||
| GENE_EXPRESSION VECTOR | VOLRUBIGENE RALAPARVOVEC TRANSGENE INSERT | 7K3J8U4MGL |