Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 07:38:45 GMT 2025
by
admin
on
Wed Apr 02 07:38:45 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT VIRUS |
| Source Materials State | LIVE NON-REPLICATING GENETICALLY MODIFIED |
| Organism Family | Parvoviridae |
| Organism Genus | Dependovirus |
| Organism Species | adeno-associated virus |
| Author | NONE |
| Infraspecific Type | SUBSTRAIN |
| Infraspecific Name | RAAV8G6PASE |
| Part | whole |
| Record UNII |
7LP92X4WPE
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Preferred Name | English | ||
|
Official Name | English | ||
|
Code | English | ||
|
Code | English | ||
|
Common Name | English | ||
|
Common Name | English | ||
|
Common Name | English | ||
|
Common Name | English | ||
|
Code | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
|
C177070
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
NO-20
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
2259927-72-3
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
100000183200
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
NO-20
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
11440
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY | |||
|
7LP92X4WPE
Created by
admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
EXPRESSED PROTEIN->VECTOR |
|
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
ACTIVE MOIETY |
for the treatment of glycogen storage disease type Ia (GSDIa)
|
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| VECTOR EXPRESSED PROTEIN | GLUCOSE-6-PHOSPHATASE | 0RJV840J55 |