U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 05:49:13 UTC 2023
Edited
by admin
on Sat Dec 16 05:49:13 UTC 2023
Nucleic Acid Subtype
Sequence Type OLIGONUCLEOTIDE
Record UNII
73D586DAMF
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
DRISAPERSEN
DASH   INN   USAN   WHO-DD  
USAN   INN  
Official Name English
GSK2402968A
Code English
PRO051
Code English
GSK-2402968
Code English
H51AON23
Code English
Drisapersen [WHO-DD]
Common Name English
DRISAPERSEN [USAN]
Common Name English
GSK 2402968A
Common Name English
drisapersen [INN]
Common Name English
GSK-2402968A
Code English
GSK2402968
Code English
PRO-051
Code English
RNA, (P-THIO)(UM-CM-AM-AM-GM-GM-AM-AM-GM-AM-UM-GM-GM-CM-AM-UM-UM-UM-CM-UM)
Common Name English
Classification Tree Code System Code
WHO-ATC M09AX04
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
Code System Code Type Description
EVMPD
SUB129424
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
NCI_THESAURUS
C166984
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
PUBCHEM
121494119
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
WIKIPEDIA
Drisapersen
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
FDA UNII
73D586DAMF
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
USAN
YY-02
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
CAS
1251830-50-8
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
DRUG BANK
DB13688
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
INN
9518
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
ChEMBL
CHEMBL2108735
Created by admin on Sat Dec 16 05:49:13 UTC 2023 , Edited by admin on Sat Dec 16 05:49:13 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-O-Methyl-Ribose 1_1-1_20 20 / 20
Linkage Site Range Site Count
Phosporothioate 1_2-1_20 19 / 19
Related Record Type Details
TARGET -> INDUCER
Completed Phase III trials and did not meet its primary endpoint. Alters the splicing of the dystrophin RNA transcript, eliminating exon 51 from the mature dystrophin mRNA.
SALT/SOLVATE -> PARENT
Related Record Type Details
ACTIVE MOIETY
Name Property Type Amount Referenced Substance Defining Parameters References
MOL_WEIGHT:NUMBER(CALCULATED) CHEMICAL