Approval Year
| Substance Class |
Nucleic Acid
Created
by
admin
on
Edited
Mon Mar 31 21:33:20 GMT 2025
by
admin
on
Mon Mar 31 21:33:20 GMT 2025
|
| Sequence Type | OLIGONUCLEOTIDE |
| Record UNII |
73D586DAMF
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| Record Status |
Validated (UNII)
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| Record Version |
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-
Download
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| Classification Tree | Code System | Code | ||
|---|---|---|---|---|
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WHO-ATC |
M09AX04
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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SUB129424
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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C166984
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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121494119
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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Drisapersen
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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73D586DAMF
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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YY-02
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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1251830-50-8
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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DB13688
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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100000155366
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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9518
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY | |||
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CHEMBL2108735
Created by
admin on Mon Mar 31 21:33:20 GMT 2025 , Edited by admin on Mon Mar 31 21:33:20 GMT 2025
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PRIMARY |
| Sugar | Site Range | Site Count |
|---|---|---|
| 2'-O-Methyl-Ribose | 1_1-1_20 | 20 / 20 |
| Linkage | Site Range | Site Count |
|---|---|---|
| Phosporothioate | 1_2-1_20 | 19 / 19 |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
TARGET -> INDUCER |
Completed Phase III trials and did not meet its primary endpoint. Alters the splicing of the dystrophin RNA transcript, eliminating exon 51 from the mature dystrophin mRNA.
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SALT/SOLVATE -> PARENT |
| Related Record | Type | Details | ||
|---|---|---|---|---|
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ACTIVE MOIETY |
| Name | Property Type | Amount | Referenced Substance | Defining | Parameters | References |
|---|---|---|---|---|---|---|
| MOL_WEIGHT:NUMBER(CALCULATED) | CHEMICAL |
|