Approval Year
| Substance Class |
Structurally Diverse
Created
by
admin
on
Edited
Wed Apr 02 17:52:18 GMT 2025
by
admin
on
Wed Apr 02 17:52:18 GMT 2025
|
| Source Materials Class | ORGANISM |
| Source Materials Type | RECOMBINANT PROTEINS |
| Organism Family | Parvoviridae |
| Organism Genus | Dependoparvovirus |
| Organism Species | adeno-associated dependoparvovirus a |
| Infraspecific Type | RECOMBINANT VECTOR |
| Infraspecific Name | AAV5-hNR2E3 |
| Part | whole |
| Record UNII |
72M7L7U43V
|
| Record Status |
Validated (UNII)
|
| Record Version |
|
-
Download
| Name | Type | Language | ||
|---|---|---|---|---|
|
Preferred Name | English | ||
|
Official Name | English | ||
|
Code | English | ||
|
Common Name | English | ||
|
Common Name | English |
| Code System | Code | Type | Description | ||
|---|---|---|---|---|---|
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C211742
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY | |||
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300000026031
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY | |||
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2964417-29-4
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY | |||
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13524
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY | |||
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MN-73
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY | |||
|
72M7L7U43V
Created by
admin on Wed Apr 02 17:52:18 GMT 2025 , Edited by admin on Wed Apr 02 17:52:18 GMT 2025
|
PRIMARY |
| Related Record | Type | Details | ||
|---|---|---|---|---|
|
|
ACTIVE MOIETY |
OCU400 is intended for the treatment of retinitis pigmentosa associated with NR2E3 and RHO
mutations.
|
Structural Modifications
| Modification Type | Location Site | Location Type | Residue Modified | Extent | Fragment Name | Fragment Approval |
|---|---|---|---|---|---|---|
| INSERTED GENE EXPRESSION VECTOR | UNSPECIFIED SUBSTANCE |
78fac1f7
(not in database)
|