U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 08:29:58 GMT 2025
Edited
by admin
on Wed Apr 02 08:29:58 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE GENETICALLY MODIFIED
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type SUBSTRAIN
Infraspecific Name AAV5-HLP-HFVIII-SQ
Part whole
Record UNII
681K1JDI8M
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
VALOCTOCOGENE ROXAPARVOVEC
INN  
USAN   INN  
Official Name English
valoctocogene roxaparvovec [INN]
Preferred Name English
ROCTAVIAN
Brand Name English
Valoctocogene roxaparvovec [WHO-DD]
Common Name English
BMN270
Code English
DNA (SYNTHETIC ADENO-ASSOCIATED VIRUS 5 VECTOR BMN 270 HUMAN BLOOD-COAGULATION FACTOR VIII SQ VARIANT-SPECIFYING)
Systematic Name English
VALROX
Brand Name English
BMN-270
Code English
VALOCTOCOGENE ROXAPARVOVEC [USAN]
Common Name English
Classification Tree Code System Code
NCI_THESAURUS C78311
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
NCI_THESAURUS C1962
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
Code System Code Type Description
DRUG BANK
DB15561
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
SMS_ID
100000183612
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
CAS
1819334-78-5
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
INN
10463
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
WIKIPEDIA
Valoctocogene roxaparvovec
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
FDA UNII
681K1JDI8M
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
NCI_THESAURUS
C152819
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
USAN
FG-90
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
DAILYMED
681K1JDI8M
Created by admin on Wed Apr 02 08:29:58 GMT 2025 , Edited by admin on Wed Apr 02 08:29:58 GMT 2025
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
GENE_EXPRESSION VECTOR VALOCTOCOGENE ROXAPARVOVEC TRANSGENE INSERT MO1EE06E1O