U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 12:35:31 GMT 2025
Edited
by admin
on Wed Apr 02 12:35:31 GMT 2025
Nucleic Acid Type VECTOR
Sequence Type COMPLETE
Record UNII
65HBD4H5PV
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
AZAMIDUGENE AUTOTEMCEL TRANSGENE INSERT
Common Name English
AZAMIDUGENE AUTOTEMCEL FOR HUMAN ALPHA-L-IDURONIDASE (IDUA)
Preferred Name English
Code System Code Type Description
FDA UNII
65HBD4H5PV
Created by admin on Wed Apr 02 12:35:31 GMT 2025 , Edited by admin on Wed Apr 02 12:35:31 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_5199 5199 / 5199
Linkage Site Range Site Count
Phosphate 1_2-1_5199 5198 / 5198