U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 19:23:12 GMT 2025
Edited
by admin
on Wed Apr 02 19:23:12 GMT 2025
Nucleic Acid Type VECTOR
Sequence Type COMPLETE
Record UNII
5EP84BHQ35
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Ciracigene golparvovec transgene insert
Preferred Name English
Code System Code Type Description
FDA UNII
5EP84BHQ35
Created by admin on Wed Apr 02 19:23:12 GMT 2025 , Edited by admin on Wed Apr 02 19:23:12 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4552 4552 / 4552
Linkage Site Range Site Count
Phosphate 1_2-1_4552 4551 / 4551
Name Property Type Amount Referenced Substance Defining Parameters References
SC ITR NUCLEIC ACID FEATURE
5' ITR NUCLEIC ACID FEATURE
bGH poly(A) NUCLEIC ACID FEATURE
CMV Enhancer NUCLEIC ACID FEATURE
bGH poly(A) NUCLEIC ACID FEATURE
CBh Promoter NUCLEIC ACID FEATURE
CBh Promoter NUCLEIC ACID FEATURE
hASPA NUCLEIC ACID FEATURE
CMV Enhancer NUCLEIC ACID FEATURE
3' ITR NUCLEIC ACID FEATURE
hASPA NUCLEIC ACID FEATURE