U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 18:51:27 UTC 2023
Edited
by admin
on Sat Dec 16 18:51:27 UTC 2023
Nucleic Acid Type RNAI
Nucleic Acid Subtype ANTI-SENSE
Sequence Type COMPLETE
Record UNII
4KM8P975UM
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Brogidirsen
INN  
Official Name English
NS 089/NCNP 02
Code English
NS-089
Code English
RNA, (P-DEOXY-P-(DIMETHYLAMINO))(2',3'-DIDEOXY-2',3'-IMINO-2',3'-SECO)(2'A->5')(M5U-M5U-G-M5U-G-M5U-C-M5U-M5U-M5U-C-M5U-M5U-C-M5U-G-M5U-M5U-A-G-C-C-A-C)
Common Name English
NS-089/NCNP-02
Code English
brogidirsen [INN]
Common Name English
NS 089/NCNP 02 (EXON 44 SKIPPING ANTISENSE OLIGONUCLEOTIDE)
Common Name English
NCNP-02
Code English
Code System Code Type Description
INN
12240
Created by admin on Sat Dec 16 18:51:27 UTC 2023 , Edited by admin on Sat Dec 16 18:51:27 UTC 2023
PRIMARY
FDA UNII
4KM8P975UM
Created by admin on Sat Dec 16 18:51:27 UTC 2023 , Edited by admin on Sat Dec 16 18:51:27 UTC 2023
PRIMARY
CAS
2409088-11-3
Created by admin on Sat Dec 16 18:51:27 UTC 2023 , Edited by admin on Sat Dec 16 18:51:27 UTC 2023
PRIMARY
NCI_THESAURUS
C190319
Created by admin on Sat Dec 16 18:51:27 UTC 2023 , Edited by admin on Sat Dec 16 18:51:27 UTC 2023
PRIMARY
Sugar Site Range Site Count
morpholino 1_1-1_24 24 / 24
Linkage Site Range Site Count
Phosphoryldimethylamine 1_2-1_24 23 / 23
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