U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 12:15:35 GMT 2025
Edited
by admin
on Wed Apr 02 12:15:35 GMT 2025
Nucleic Acid Type PLASMID
Sequence Origin HUMAN
Sequence Type COMPLETE
Record UNII
3CLT8HFQ3Q
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
Alvamemugene sulseparvovec transgene insert
Common Name English
LB-001 transgene insert
Preferred Name English
Code System Code Type Description
FDA UNII
3CLT8HFQ3Q
Created by admin on Wed Apr 02 12:15:35 GMT 2025 , Edited by admin on Wed Apr 02 12:15:35 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4615 4615 / 4615
Linkage Site Range Site Count
Phosphate 1_2-1_4615 4614 / 4614
Name Property Type Amount Referenced Substance Defining Parameters References
5’ Inverted terminal repeat (ITR) NUCLEIC ACID FEATURE
2A NUCLEIC ACID FEATURE
3’ Inverted terminal repeat (ITR) NUCLEIC ACID FEATURE
3’ Human Albumin homologous arm NUCLEIC ACID FEATURE
MUT NUCLEIC ACID FEATURE
5’ Human Albumin homologous arm NUCLEIC ACID FEATURE