U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 16:04:47 UTC 2023
Edited
by admin
on Sat Dec 16 16:04:47 UTC 2023
Nucleic Acid Type OLIGONUCLEOTIDE
Nucleic Acid Subtype
Sequence Type COMPLETE
Record UNII
31N550RD05
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
DANVATIRSEN
INN  
Official Name English
ALL-P-AMBO-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-5-METHYL-PTHIOCYTIDYLYL-(3'->5')-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-5-METHYL-P-THIOURIDYLYL-(3'->5')-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-P-THIOADENYLYL-(3'->5')-P-THIOTHYMIDYLYL-(3'->5')-PTHIOTHYMIDYLYL-(3'->5')-P-T
Common Name English
danvatirsen [INN]
Common Name English
ISIS-481464
Code English
Danvatirsen [WHO-DD]
Common Name English
ISIS-STAT3RX
Code English
DANVATIRSEN [USAN]
Common Name English
AZD9150
Code English
ALL-P-AMBO-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-5-METHYL-P-THIOCYTIDYLYL-(3'->5')-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-5-METHYL-P-THIOURIDYLYL-(3'->5')-2'-O,4'-C-((1S)-2-ETHANE-1,1-DIYL)-P-THIOADENYLYL-(3'->5')-P-THIOTHYMIDYLYL-(3'->5')-P-THIOTHYMIDYLYL-(3'->5')
Systematic Name English
AZD-9150
Code English
DNA, D(P-THIO)(((5'.XI.)-2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-LYXO-HEXOFURANO)M5C-(3'->4')-((5'.XI.)-2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-LYXO-HEXOFURANO)M5U-(3'->4')-((5'.XI.)-2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)
Systematic Name English
Classification Tree Code System Code
NCI_THESAURUS C1291
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
Code System Code Type Description
CAS
1402357-06-5
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
INN
10612
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
FDA UNII
31N550RD05
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
DRUG BANK
DB14825
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
USAN
FG-83
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
NCI_THESAURUS
C101368
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
PRIMARY
CAS
1402100-56-4
Created by admin on Sat Dec 16 16:04:47 UTC 2023 , Edited by admin on Sat Dec 16 16:04:47 UTC 2023
SUPERSEDED
Sugar Site Range Site Count
Deoxyribose (DNA) 1_4-1_13 10 / 16
2,'4'-locked-Ribose (alpha-L-LNA) 1_1-1_3;1_14-1_16 6 / 16
Linkage Site Range Site Count
Phosporothioate 1_2-1_16 15 / 15
Related Record Type Details
SALT/SOLVATE -> PARENT
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
NUCLEOSIDE BASE SUBSTITUTION [1_1] [1_16] SITE_SPECIFIC 5-METHYLDEOXYCYTIDINE B200GV71QM