U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Wed Apr 02 03:46:53 GMT 2025
Edited
by admin
on Wed Apr 02 03:46:53 GMT 2025
Source Materials Class ORGANISM
Source Materials Type RECOMBINANT VIRUS
Source Materials State LIVE NON-REPLICATING
Organism Family Parvoviridae
Organism Genus Dependovirus
Organism Species adeno-associated virus
Author NONE
Infraspecific Type SUBSTRAIN
Infraspecific Name rAAV2-hAADC
Part whole
Record UNII
2WRS0PE04O
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
NBIB-1817
Preferred Name English
EZALADCIGENE RESOPARVOVEC
INN   USAN  
Official Name English
RAAV2-HAADC (RECOMBINANT ADENO-ASSOCIATED VIRUS TYPE 2-HUMAN AROMATIC L-AMINO ACID DECARBOXYLASE)
Common Name English
EZALADCIGENE RESOPARVOVEC [USAN]
Common Name English
ezaladcigene resoparvovec [INN]
Common Name English
VY-AADC02
Code English
Code System Code Type Description
FDA UNII
2WRS0PE04O
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
CAS
2226647-27-2
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
NCI_THESAURUS
C171799
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
INN
11098
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
SMS_ID
300000010801
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
USAN
HI-186
Created by admin on Wed Apr 02 03:46:53 GMT 2025 , Edited by admin on Wed Apr 02 03:46:53 GMT 2025
PRIMARY
Related Record Type Details
EXPRESSED PROTEIN->VECTOR
TARGET->ENZYME REPLACEMENT
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
INSERTED GENE EXPRESSION VECTOR EZALADCIGENE RESOPARVOVEC TRANSGENE INSERT 9GTR4QHK6A