U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 14:08:29 UTC 2023
Edited
by admin
on Sat Dec 16 14:08:29 UTC 2023
Source Materials Class ORGANISM
Source Materials Type VIRUS
Source Materials State LIVE GENETICALLY MODIFIED NON-REPLICATING
Organism Family Parvoviridae
Organism Genus Dependoparvovirus
Organism Species adeno-associated dependoparvovirus a
Infraspecific Type RECOMBINANT VECTOR
Infraspecific Name AAV-2-HRPE65V2
Part WHOLE
Record UNII
2SPI046IKD
Record Status Validated (UNII)
Record Version
  • Download
Related Record Type
Name Type Language
VORETIGENE NEPARVOVEC
INN   USAN   WHO-DD  
USAN   INN  
Official Name English
VORETIGENE NEPARVOVEC [USAN]
Common Name English
voretigene neparvovec [INN]
Common Name English
ADENO-ASSOCIATED VIRUS SEROTYPE 2 VECTOR CONTAINING THE HUMAN RETINAL PIGMENT EPITHELIUM 65KD A PROTEIN (RPE65) GENE
Common Name English
AAV2-HRPE65V2
Code English
AAV-2-HRPE65V2
Code English
VORETIGENE NEPARVOVEC [WHO-DD]
Common Name English
Classification Tree Code System Code
NCI_THESAURUS C61199
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
NCI_THESAURUS C1962
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
Code System Code Type Description
ChEMBL
CHEMBL3707275
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
NCI_THESAURUS
C152915
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
CAS
1646819-03-5
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
FDA UNII
2SPI046IKD
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
RXCUI
1995538
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
ALTERNATIVE
EVMPD
SUB182301
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
INN
10403
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
RXCUI
1995537
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
DRUG BANK
DB13932
Created by admin on Sat Dec 16 14:08:29 UTC 2023 , Edited by admin on Sat Dec 16 14:08:29 UTC 2023
PRIMARY
Related Record Type Details
SUB_CONCEPT->SUBSTANCE
Related Record Type Details
ACTIVE MOIETY
Name Property Type Amount Referenced Substance Defining Parameters References
MOL_WEIGHT:NUMBER(CALCULATED) CHEMICAL