U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Wed Apr 02 10:50:41 GMT 2025
Edited
by admin
on Wed Apr 02 10:50:41 GMT 2025
Nucleic Acid Type GENE
Sequence Origin HUMAN
Sequence Type COMPLETE
Record UNII
2S4PWR7ZEU
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
VANGLUSAGENE ENSIPARVOVEC TRANSGENE INSERT
Preferred Name English
Code System Code Type Description
FDA UNII
2S4PWR7ZEU
Created by admin on Wed Apr 02 10:50:41 GMT 2025 , Edited by admin on Wed Apr 02 10:50:41 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_1-1_4679 4679 / 4679
Linkage Site Range Site Count
Phosphate 1_2-1_4679 4678 / 4678
Name Property Type Amount Referenced Substance Defining Parameters References
ApoE HCR1 enhancer NUCLEIC ACID FEATURE
Modified HBB2 intron NUCLEIC ACID FEATURE
Bovine Growth Hormone PolyA NUCLEIC ACID FEATURE
3’ ITR NUCLEIC ACID FEATURE
Codon optimized secretable GAA NUCLEIC ACID FEATURE
hAAT promoter NUCLEIC ACID FEATURE
5’ ITR NUCLEIC ACID FEATURE