Rivunatpagene Miziparvovec

Approval Year

Substance Class	Structurally Diverse Created by `admin` on `Wed Apr 02 10:55:02 GMT 2025` Edited by `admin` on `Wed Apr 02 10:55:02 GMT 2025`
Source Materials Class	ORGANISM
Source Materials Type	RECOMBINANT VIRUS
Source Materials State	LIVE NON-REPLICATING GENETICALLY MODIFIED
Organism Family	Parvoviridae
Organism Genus	Dependoparvovirus
Organism Species	adeno-associated dependoparvovirus a
Infraspecific Type	RECOMBINANT VECTOR
Infraspecific Name	AAV9. ATP7B-MBD456
Part	whole
Record UNII	24Q8LJQ6Y2
Record Status	`Validated (UNII)`
Record Version

Download

Name

Type

Language

UX701

Preferred Name

English

Rivunatpagene Miziparvovec

Official Name

English

DNA (recombinant replication-defective adeno-associated virus serotype 9 vector UX701 murine transthyretin enhancer plus human transthyretin promoter plus simian virus 40 intron plus human adenosine triphosphatase copper-transporting ? metal-binding doma

Common Name

English

recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding ATPase copper-transporting beta gene (ATP7B, copper transporting ATPase 2), modified to encode the last three of the six metal-binding domains (ATP7B-MBD456), under co

Common Name

English

rivunatpagene miziparvovec [INN]

Common Name

English

UX-701

Common Name

English

RIVUNATPAGENE MIZIPARVOVEC [USAN]

Common Name

English

Code System Code Type Description

SMS_ID

300000023114