U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Structurally Diverse
Created
by admin
on Sat Dec 16 15:08:02 GMT 2023
Edited
by admin
on Sat Dec 16 15:08:02 GMT 2023
Source Materials Class ORGANISM
Source Materials Type AUTOLOGOUS HUMAN
Source Materials State LIVE GENETICALLY MODIFIED
Source Materials Parent
Part SKIN
Fraction Material Type CELLS
Fraction Name FIBROBLAST
Record UNII
0S9A4XK1WT
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
DABOCEMAGENE AUTOFICEL
INN   USAN  
Official Name English
DNA (RECOMBINANT LENTIVIRUS VECTOR INXN-2004-TRANSDUCED HUMAN AUTOLOGOUS DYSTROPHIC EPIDERMOLYSIS BULLOSA DERMAL FIBROBLAST CELL FCX-007 INTEGRATED PROVIRAL HUMAN COLLAGEN TYPE VII TRANSGENE COL7A1 PLUS 5'-HUMAN CYTOMEGALOVIRUS PROMOTER/UTR-AND 3'-LTR/PO
Common Name English
AUTOLOGOUS HUMAN DERMAL FIBROBLAST CELLS DERIVED FROM SKIN BIOPSIES, AND TRANSDUCED WITH A NON-REPLICATING, SELF-INACTIVATING LENTIVIRUS VECTOR THAT ENCODES HUMAN COLLAGEN TYPE VII ALPHA 1 (COL7A1) UNDER THE CONTROL OF A HUMAN CYTOMEGALOVIRUS (CMV) PROMO
Common Name English
dabocemagene autoficel [INN]
Common Name English
DABOCEMAGENE AUTOFICEL [USAN]
Common Name English
FCX-007
Code English
Code System Code Type Description
FDA UNII
0S9A4XK1WT
Created by admin on Sat Dec 16 15:08:02 GMT 2023 , Edited by admin on Sat Dec 16 15:08:02 GMT 2023
PRIMARY
INN
11676
Created by admin on Sat Dec 16 15:08:02 GMT 2023 , Edited by admin on Sat Dec 16 15:08:02 GMT 2023
PRIMARY
USAN
HI-151
Created by admin on Sat Dec 16 15:08:02 GMT 2023 , Edited by admin on Sat Dec 16 15:08:02 GMT 2023
PRIMARY
NCI_THESAURUS
C180642
Created by admin on Sat Dec 16 15:08:02 GMT 2023 , Edited by admin on Sat Dec 16 15:08:02 GMT 2023
PRIMARY
CAS
2365353-63-3
Created by admin on Sat Dec 16 15:08:02 GMT 2023 , Edited by admin on Sat Dec 16 15:08:02 GMT 2023
PRIMARY
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
VECTOR EXPRESSED PROTEIN COLLAGEN ALPHA-1(VII) CHAIN 1AH5NN82CT