AGANIRSEN

U.S. Department of Health & Human Services Divider Arrow

National Institutes of Health Divider Arrow

NCATS

Investigational

Investigational

Approval Year

Substance Class	Nucleic Acid Created by `admin` on `Mon Mar 31 20:59:23 GMT 2025` Edited by `admin` on `Mon Mar 31 20:59:23 GMT 2025`
Sequence Type	OLIGONUCLEOTIDE
Record UNII	0N3FY8225K
Record Status	`Validated (UNII)`
Record Version

Download

Name

Type

Language

AGANIRSEN

Official Name

English

aganirsen [INN]

Preferred Name

English

(3'->5')D(P-THIO)(T-A-T-C-C-G-G-A-G-G-G-C-T-C-G-C-C-A-T-G-C-T G-C-T)

Common Name

English

Aganirsen [WHO-DD]

Common Name

English

GS-101

Common Name

English

Classification Tree Code System Code

FDA ORPHAN DRUG

500515

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

NCI_THESAURUS

C1291

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

EU-Orphan Drug

EU/03/14/1275

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

NCI_THESAURUS

C29639

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

NCI_THESAURUS

C1742

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

Code System Code Type Description

ChEMBL

CHEMBL2108296

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

FDA UNII

0N3FY8225K

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

NCI_THESAURUS

C148131

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

WIKIPEDIA

Aganirsen

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

EVMPD

SUB129665

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

INN

9122

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

CAS

1146887-67-3

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

SMS_ID

100000155629

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

DRUG BANK

DB15369

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

EPA CompTox

DTXSID801336080

Created by admin on Mon Mar 31 20:59:23 GMT 2025 , Edited by admin on Mon Mar 31 20:59:23 GMT 2025

PRIMARY

Sugar	Site Range	Site Count
Deoxyribose (DNA)	1_1-1_25	25 / 25

Linkage	Site Range	Site Count
Phosporothioate	1_2-1_25	24 / 24

Name	Property Type	Amount	Referenced Substance	Defining	Parameters	References
MOL_WEIGHT:NUMBER(CALCULATED)	CHEMICAL