U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Substance Class Nucleic Acid
Created
by admin
on Sat Dec 16 13:27:14 UTC 2023
Edited
by admin
on Sat Dec 16 13:27:14 UTC 2023
Nucleic Acid Type OLIGONUCLEOTIDE
Nucleic Acid Subtype
Sequence Type COMPLETE
Record UNII
0IEO0F56LV
Record Status Validated (UNII)
Record Version
  • Download
Name Type Language
INOTERSEN
INN   USAN   WHO-DD  
INN   USAN  
Official Name English
INOTERSEN [MI]
Common Name English
Inotersen [WHO-DD]
Common Name English
inotersen [INN]
Common Name English
ISIS-420915
Code English
GSK-2998728
Code English
INOTERSEN [USAN]
Common Name English
ISIS 420915
Code English
Classification Tree Code System Code
FDA ORPHAN DRUG 374512
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
Code System Code Type Description
RXCUI
2099289
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
CAS
1492984-65-2
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
WIKIPEDIA
Inotersen
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
DRUG CENTRAL
5319
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
INN
10294
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
DAILYMED
0IEO0F56LV
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
MERCK INDEX
m12102
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
FDA UNII
0IEO0F56LV
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
USAN
CD-06
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
DRUG BANK
DB14713
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
EPA CompTox
DTXSID501027905
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
PUBCHEM
121492004
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
NCI_THESAURUS
C121667
Created by admin on Sat Dec 16 13:27:14 UTC 2023 , Edited by admin on Sat Dec 16 13:27:14 UTC 2023
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_6-1_15 10 / 20
2'-O-Methoxyethyl ribose 1_1-1_5;1_16-1_20 10 / 20
Linkage Site Range Site Count
Phosporothioate 1_2-1_20 19 / 19
Related Record Type Details
SALT/SOLVATE -> PARENT
TARGET->INHIBITOR OF EXPRESSION
TARGET->INHIBITOR OF EXPRESSION
Related Record Type Details
ACTIVE MOIETY

Structural Modifications

Modification Type Location Site Location Type Residue Modified Extent Fragment Name Fragment Approval
NUCLEOSIDE SUBSTITUTION [1_2] [1_18] [1_19] [1_20] C 2'-O-(2-METHOXYETHYL)-5-METHYLCYTIDINE AOQ54IZZ6J
NUCLEOSIDE SUBSTITUTION [1_10] C 5-METHYLDEOXYCYTIDINE B200GV71QM
NUCLEOSIDE SUBSTITUTION [1_1] [1_3] [1_4] [1_17] U 2'-O-(2-METHOXYETHYL)-5-METHYLURIDINE 9Q36I4D9VB