DNA (recombinant adeno-associated virus 9 vector TSHA-120 synthetic JeT promoter plus human gigaxonin transgene plus synthetic polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks-specifying)
Preferred Name
English
Tidagixagene Derxeparvovec
Official Name
English
TSHA-120
Common Name
English
recombinant, self-complementary (dimeric), non-replicating adeno-associated virus serotype 9 (scAAV9) vector encoding codon-optimised human gigaxonin (giant axonal neuropathy [GAN] gene, Kelch-like protein 16) under the control of the artificial JeT prom
