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Approval Year

Unknown
149124
Name Type Language
DNA (recombinant adeno-associated virus 9 vector TSHA-120 synthetic JeT promoter plus human gigaxonin transgene plus synthetic polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks-specifying)
Preferred Name English
Tidagixagene Derxeparvovec
INN  
Official Name English
TSHA-120
Common Name English
recombinant, self-complementary (dimeric), non-replicating adeno-associated virus serotype 9 (scAAV9) vector encoding codon-optimised human gigaxonin (giant axonal neuropathy [GAN] gene, Kelch-like protein 16) under the control of the artificial JeT prom
Common Name English
tidagixagene derxeparvovec [INN]
Common Name English
Code System Code Type Description
FDA UNII
Y7ARS22SWQ
Created by admin on Wed Apr 02 15:40:42 GMT 2025 , Edited by admin on Wed Apr 02 15:40:42 GMT 2025
PRIMARY
CAS
2644621-85-0
Created by admin on Wed Apr 02 15:40:42 GMT 2025 , Edited by admin on Wed Apr 02 15:40:42 GMT 2025
PRIMARY
NCI_THESAURUS
C190499
Created by admin on Wed Apr 02 15:40:42 GMT 2025 , Edited by admin on Wed Apr 02 15:40:42 GMT 2025
PRIMARY
SMS_ID
300000039048
Created by admin on Wed Apr 02 15:40:42 GMT 2025 , Edited by admin on Wed Apr 02 15:40:42 GMT 2025
PRIMARY
INN
12310
Created by admin on Wed Apr 02 15:40:42 GMT 2025 , Edited by admin on Wed Apr 02 15:40:42 GMT 2025
PRIMARY
NIH
NCATS
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