U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
ENGABEXAGENE CINCESPARVOVEC
Common Name English
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR, ENCODING CODON-OPTIMISED HUMAN .BETA.-HEXOSAMINIDASE SUBUNITS .BETA. AND .ALPHA., JOINED BY A PORCINE TESCHOVIRUS 2A PEPTIDE LINKER, UNDER CONTROL OF A SYNTHETIC PROMOTER (CYT
Common Name English
engabexagene cincesparvovec [INN]
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR TSHA-101 SYNTHETIC CAG PROMOTER PLUS HUMAN .BETA.-N-ACETYLHEXOSAMINIDASE SUBUNIT .BETA. PRECURSOR FUSION PROTEIN WITH PORCINE TESCHOVIRUS 2A PEPTIDE FUSION PROTEIN WITH HUMAN .BETA.-N-ACETYLHEXOSAMINIDASE SU
Common Name English
Code System Code Type Description
INN
12045
Created by admin on Sat Dec 16 18:47:35 UTC 2023 , Edited by admin on Sat Dec 16 18:47:35 UTC 2023
PRIMARY
FDA UNII
XX923BN5NY
Created by admin on Sat Dec 16 18:47:35 UTC 2023 , Edited by admin on Sat Dec 16 18:47:35 UTC 2023
PRIMARY
NCI_THESAURUS
C188657
Created by admin on Sat Dec 16 18:47:35 UTC 2023 , Edited by admin on Sat Dec 16 18:47:35 UTC 2023
PRIMARY
CAS
2567881-77-8
Created by admin on Sat Dec 16 18:47:35 UTC 2023 , Edited by admin on Sat Dec 16 18:47:35 UTC 2023
PRIMARY