U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
ENGABEXAGENE CINCESPARVOVEC
Common Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR TSHA-101 SYNTHETIC CAG PROMOTER PLUS HUMAN .BETA.-N-ACETYLHEXOSAMINIDASE SUBUNIT .BETA. PRECURSOR FUSION PROTEIN WITH PORCINE TESCHOVIRUS 2A PEPTIDE FUSION PROTEIN WITH HUMAN .BETA.-N-ACETYLHEXOSAMINIDASE SU
Preferred Name English
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR, ENCODING CODON-OPTIMISED HUMAN .BETA.-HEXOSAMINIDASE SUBUNITS .BETA. AND .ALPHA., JOINED BY A PORCINE TESCHOVIRUS 2A PEPTIDE LINKER, UNDER CONTROL OF A SYNTHETIC PROMOTER (CYT
Common Name English
engabexagene cincesparvovec [INN]
Common Name English
Code System Code Type Description
INN
12045
Created by admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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FDA UNII
XX923BN5NY
Created by admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
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NCI_THESAURUS
C188657
Created by admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
PRIMARY
CAS
2567881-77-8
Created by admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
PRIMARY
SMS_ID
300000032081
Created by admin on Wed Apr 02 12:16:20 GMT 2025 , Edited by admin on Wed Apr 02 12:16:20 GMT 2025
PRIMARY
NIH
NCATS
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