U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
COFIRASERSEN
USAN  
Official Name English
IONIS-ENACRX
Code English
DNA, D(P-THIO)((2'-O,4'-C-((S)-ETHYLIDENE))M5RC-(2'-O,4'-C-((S)-ETHYLIDENE))M5RC-(2'-O,4'-C-((S)-ETHYLIDENE))M5RC-G-A-T-A-G-M5C-T-G-G-T-(2'-O,4'-C-((S)-ETHYLIDENE))M5RU-(2'-O,4'-C-((S)-ETHYLIDENE))RG-(2'-O,4'-C-((S)-ETHYLIDENE))M5RU)
Common Name English
DNA, D(P-THIO)((2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-MANNOFURANO)M5C-(3'->4')-(2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-MANNOFURANO)M5C-(3'->4')-(2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-MANNOFURANO)M5C-G-A-T-A-
Common Name English
COFIRASERSEN [USAN]
Common Name English
ION-827359
Code English
cofirasersen [INN]
Common Name English
Code System Code Type Description
INN
11517
Created by admin on Sat Dec 16 16:12:46 GMT 2023 , Edited by admin on Sat Dec 16 16:12:46 GMT 2023
PRIMARY
CAS
2247669-96-9
Created by admin on Sat Dec 16 16:12:46 GMT 2023 , Edited by admin on Sat Dec 16 16:12:46 GMT 2023
PRIMARY
NCI_THESAURUS
C179078
Created by admin on Sat Dec 16 16:12:46 GMT 2023 , Edited by admin on Sat Dec 16 16:12:46 GMT 2023
PRIMARY
FDA UNII
XV92IM2BG0
Created by admin on Sat Dec 16 16:12:46 GMT 2023 , Edited by admin on Sat Dec 16 16:12:46 GMT 2023
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_4-1_13 10 / 16
2'-O,4'-ethylene bridged Ribose 1_1-1_3;1_14-1_16 6 / 16
Linkage Site Range Site Count
Phosporothioate 1_2-1_16 15 / 15