U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
FIROLIMOGENE AUTOTEMCEL
INN  
Official Name English
AUTOLOGOUS CD34+ CELLS ISOLATED FROM BONE MARROW OF NEWLY DIAGNOSED X-LINKED SEVERE COMBINED IMMUNODEFICIENCY (X-SCID) PATIENTS, TRANSDUCED EX VIVO WITH A SELF-INACTIVATING LENTIVIRAL VECTOR, ENCODING CODON-OPTIMIZED HUMAN INTERLEUKIN-2 RECEPTOR SUBUNIT
Preferred Name English
firolimogene autotemcel [INN]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 759720
Created by admin on Wed Apr 02 11:16:00 GMT 2025 , Edited by admin on Wed Apr 02 11:16:00 GMT 2025
Code System Code Type Description
SMS_ID
300000015441
Created by admin on Wed Apr 02 11:16:00 GMT 2025 , Edited by admin on Wed Apr 02 11:16:00 GMT 2025
PRIMARY
FDA UNII
XH2XT2GQS6
Created by admin on Wed Apr 02 11:16:00 GMT 2025 , Edited by admin on Wed Apr 02 11:16:00 GMT 2025
PRIMARY
INN
11551
Created by admin on Wed Apr 02 11:16:00 GMT 2025 , Edited by admin on Wed Apr 02 11:16:00 GMT 2025
PRIMARY
NCI_THESAURUS
C184824
Created by admin on Wed Apr 02 11:16:00 GMT 2025 , Edited by admin on Wed Apr 02 11:16:00 GMT 2025
PRIMARY
NIH
NCATS
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