U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
BEVUFENOGENE NOFEPARVOVEC
INN   USAN  
Official Name English
HMI-102
Preferred Name English
DNA (RECOMBINANT HUMAN HEMATOPOIETIC STEM CELL-DERIVED ADENO-ASSOCIATED VIRUS VECTOR SEROTYPE AAVHSC15 HUMAN LIVER-SPECIFIC EXPRESSION CASSETTE INCLUDING HUMAN PHENYLALANINE 4-HYDROXYLASE CODON-OPTIMIZED CDNA PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMIN
Common Name English
A NON-REPLICATING, RECOMBINANT ADENO-ASSOCIATED VIRUS, HEMATOPOIETIC STEM CELL SEROTYPE 15 (AAVHSC15) EXPRESSING CODON-OPTIMISED HUMAN PHENYLALANINE HYDROXYLASE (PAH) UNDER CONTROL OF A LIVER-SPECIFIC HYBRID PROMOTER (COMPRISING HUMAN HEPATIC CONTROL REG
Common Name English
bevufenogene nofeparvovec [INN]
Common Name English
BEVUFENOGENE NOFEPARVOVEC [USAN]
Common Name English
Code System Code Type Description
USAN
JK-252
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY
NCI_THESAURUS
C179075
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY
INN
11521
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY INN
FDA UNII
W6GL3Z8KWT
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY
CAS
2374772-30-0
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY
SMS_ID
100000178095
Created by admin on Wed Apr 02 08:02:46 GMT 2025 , Edited by admin on Wed Apr 02 08:02:46 GMT 2025
PRIMARY
NIH
NCATS
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