U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
IFEZUNTIRGENE INILPARVOVEC
INN  
Official Name English
A RECOMBINANT, REPLICATION DEFICIENT ADENO-ASSOCIATED VIRUS SEROTYPE 5 (AAV5) VECTOR ENCODING A MICRORNA (MIRNA) TARGETING THE EXON 1 OF HUMAN HUNTINGTIN PROTEIN (HTT) MRNA (MIHTT). THE EXPRESSION CASSETTE CONSISTS OF A CHIMERIC CHICKEN BETA-ACTIN PROMOT
Preferred Name English
DNA (RECOMBINANT REPLICATION-DEFICIENT ADENO-ASSOCIATED VIRUS 5 VECTOR AMT-130 CHICKEN .BETA.-ACTIN PROMOTER PLUS HUMAN HUNTINGTIN MRNA-TARGETING MICRORNA MIHTT-SPECIFYING)
Common Name English
ifezuntirgene inilparvovec [INN]
Common Name English
Code System Code Type Description
CLINICAL_TRIALS.GOV
NCT04120493
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
NON-SPECIFIC SUBSTITUTION
FDA UNII
VB2ZC1P6P4
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
PRIMARY
CAS
2407582-19-6
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
PRIMARY
INN
11711
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
PRIMARY
SMS_ID
100000183885
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
PRIMARY
NCI_THESAURUS
C184855
Created by admin on Wed Apr 02 05:46:06 GMT 2025 , Edited by admin on Wed Apr 02 05:46:06 GMT 2025
PRIMARY